News About DMD » FED sponsors an international workshop
FED sponsors an international workshop
FED sponsors an international workshop on exon skipping approaches in Duchenne dystrophy.
A workshop was organized by Eric Hoffman at Children's National Medical Center to discuss progress towards human clinical trials in exon-skipping approaches in Duchenne dystrophy. Judith Vandeutekom and Prosensa described their success of local muscle injections in patient with DMD. AVI and Dr. Francesco Muntoni described their progress towards a morpholino clinical trial. Drs. Hoffman, Partridge, and Takeda showed their success in systemic delivery in naturally-occurring dogs with Duchenne dystrophy. Approximately 40 invitees attended the workshop, including representatives from NIH, FED, and FDA.
